Tag Archives: Preclinical

Expanding its preclinical attack on Duchenne MD, Sarepta grabs a license for Duke’s CRISPR tech – ENDPOINTS NEWS

Sarepta $SRPT announced this morning that it’s teaming up with Duke University to explore new CRISPR-based methods in the hunt for an effective Duchenne muscular dystrophy therapy. The company says… Read more »

Capricor Therapeutics Reports Intravenous Administration of CAP-1002 Shown to be Effective in Preclinical Models of Duchenne Muscular Dystrophy

LA JOLLA, Calif., Oct. 6, 2017 /PRNewswire/ — Capricor Therapeutics, Inc. (NASDAQ: CAPR), in a poster presentation at the Alliance for Regenerative Medicine’s Cell and Gene Meeting on the Mesa,… Read more »

Biophytis Clinical Stage Drug-Candidate Sarconeos Demonstrates Efficacy in Preclinical Models of Duchenne Muscular Dystrophy

Biophytis announces abstract accepted at World Muscle Society international congress (3-7 October 2017, St Malo, France) Duchenne muscular dystrophy is a new Orphan indication for Sarconeos … Read more »

New Preclinical Data Support SGT-001 As A Novel Treatment Approach For Duchenne Muscular Dystrophy

CAMBRIDGE, Mass.–(BUSINESS WIRE)–Solid Biosciences announced today that new data from two preclinical studies reinforce the potential of its investigational microdystrophin gene therapy, SGT-001, to be an effective treatment approach for… Read more »

GTx Announces Results from Preclinical Studies of SARMs in Duchenne Muscular Dystrophy Models Published in Human Molecular Genetics

MEMPHIS, Tenn.–(BUSINESS WIRE)–GTx, Inc. (Nasdaq: GTXI) today announced the publication in the journal Human Molecular Genetics of results from preclinical studies supporting the potential efficacy of the Company’s SARMs, and… Read more »